[1
]Department of Pediatrics, Aflac Cancer and Blood Disorders, Atlanta, Georgia, USA
[2
]Hemophilia of Georgia Center for Bleeding and Clotting Disorders, Atlanta, Georgia,
USA
[3
]Pediatric Hematology Oncology, St. Jude Affiliate Clinic at Novant Health Hemby Children’s
Hospital, Charlotte, North Carolina, USA
[4
]National Hemophilia Foundation, New York, New York, USA
[5
]Department of Pediatrics, Washington University in St. Louis, St. Louis, Missouri,
USA
[6
]Hematology/Oncology Department, Washington University in St. Louis, St. Louis, Missouri,
USA
[7
]Takeda Pharmaceuticals U.S.A, Lexington, Massachusetts, USA
[8
]Indiana Hemophilia and Thrombosis Center, Indianapolis, Indiana, USA
[9
]Hemophilia Federation of America, Washington, DC, USA
[10
]Hemophilia of Georgia, Atlanta, Georgia
[11
]Department of Pediatrics, Children’s Hospital Los Angeles, Los Angeles, California,
USA
[12
]Keck School of Medicine, University of Southern California, Los Angeles, California,
USA
[13
]East Carolina University Hemophilia Treatment Center, Greenville, North Carolina,
USA
[14
]Division of Hematology, UNC Blood Research Center, University of North Carolina at
Chapel Hill, Chapel Hill, North Carolina, USA
[15
]Washington Center for Bleeding Disorders, Seattle, Washington, USA
[16
]Mary M. Gooley Hemophilia Center, Rochester, New York, USA
[17
]Blood Center of Wisconsin, Versiti, Milwaukee, Wisconsin, USA
[18
]Department of Pediatrics, Medical College of Wisconsin, Milwaukee, Wisconsin, USA
[19
]Hemophilia and Thrombosis Center, University of Colorado Denver, Denver, Colorado,
USA
[20
]Department of Bioengineering, University of Colorado Denver, Denver, Colorado, USA
[21
]Department of Pediatrics, University of Colorado Denver, Denver, Colorado, USA
[22
]Department of pediatrics, Anschutz Medical Campus, Aurora, Colorado, USA
[23
]National Heart and Lung Institute, Imperial College, London, UK
[24
]Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati,
Ohio, USA
[25
]Pediatrics, Cincinnati Children’s Hospital Medical Center, Cincinnati, Ohio, USA
[26
]Children’s Healthcare of Atlanta, Atlanta, Georgia, USA
[27
]Division of Pediatric Genetics, Department of Pediatrics, University of Florida College
of Medicine-Jacksonville, Jacksonville, Florida, USA