[1
]Center for Inherited Blood Disorders, Orange, California, USA
[2
]Pediatric Hematology Division, Department of Pediatrics, University of California
at Irvine, Children's Hospital of Orange County, Irvine, California, USA
[3
]Hemostasis and Thrombosis Center, Northwell Health, New Hyde Park, New York, New York,
USA
[4
]Center for Bleeding and Clotting Disorders, M Health Fairview, Minneapolis, Minnesota,
USA
[5
]Ultragenyx Pharmaceutical Inc Novato, California, USA
[6
]Plasminogen Deficiency Foundation, Durham, North Carolina, USA
[7
]National Hemophilia Foundation, New York, New York, USA
[8
]Sigilon Therapeutics, Cambridge, Massachusetts, USA
[9
]Patient author, Lived Experience Expert, Dearborn, Michigan, USA
[10
]Hamilton Regional Laboratory Medicine Program, Hamilton Health Sciences, Hamilton,
Ontario, Canada
[11
]Department of Pathology and Molecular Medicine, McMaster University, Hamilton, Ontario,
Canada
[12
]Center for Biologics Evaluation and Research, U.S. Food and Drug Administration, Silver
Spring, Maryland, USA
[13
]Angelo Bianchi Bonomi Hemophilia and Thrombosis Center and Fondazione Luigi Villa,
Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy
[14
]Oncology Support Service, Providence Alaska Medical Center, Anchorage, Alaska, USA
[15
]Department of Pathophysiology and Transplantation, Università degli Studi di Milano,
Milan, Italy
[16
]Comprehensive Hemophilia Center, Division of Hematology, Mayo Clinic, Rochester, Minnesota,
USA
[17
]American Thrombosis and Hemostasis Network, Rochester, New York, USA
[18
]The Hemophilia Center, Oregon Health & Science University, Portland, Oregon, USA
[19
]Hemab Therapeutics, Copenhagen, Denmark
[20
]Bleeding and Clotting Disorders Institute, Peoria, Illinois, USA
[21
]Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel
Hill, Chapel Hill, North Carolina, USA
[22
]UNC Blood Research Center, University of North Carolina at Chapel Hill, Chapel Hill,
North Carolina, USA
[23
]Indiana Hemophilia and Thrombosis Center, Indianapolis, Indiana, USA