ScienceOpen:
research and publishing network
For Publishers
Discovery
Metadata
Peer review
Hosting
Publishing
For Researchers
Join
Publish
Review
Collect
My ScienceOpen
Sign in
Register
Dashboard
Blog
About
Search
Advanced search
My ScienceOpen
Sign in
Register
Dashboard
Search
Search
Advanced search
For Publishers
Discovery
Metadata
Peer review
Hosting
Publishing
For Researchers
Join
Publish
Review
Collect
Blog
About
36
views
0
references
Top references
cited by
207
Cite as...
0 reviews
Review
0
comments
Comment
0
recommends
+1
Recommend
0
collections
Add to
0
shares
Share
Twitter
Sina Weibo
Facebook
Email
1,656
similar
All similar
Record
: found
Abstract
: not found
Article
: not found
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study
Author(s):
Richard Finkel
,
Claudia A. Chiriboga
,
Jiri Vajsar
,
John Day
,
Jacqueline Montes
,
Darryl De Vivo
,
Mason Yamashita
,
Frank Rigo
,
Gene Hung
,
Eugene Schneider
,
Daniel A. Norris
,
Shuting Xia
,
C Frank Bennett
,
Kathie Bishop
Publication date:
2016-12-01
Journal:
The Lancet
Publisher:
Elsevier BV
Read this article at
ScienceOpen
Publisher
Cite as...
There is no author summary for this article yet. Authors can add summaries to their articles on ScienceOpen to make them more accessible to a non-specialist audience.
Related collections
NTT Journal for Theology and the Study of Religion
Author and article information
Journal
DOI::
10.1016/S0140-6736(16)31408-8
License:
http://www.elsevier.com/tdm/userlicense/1.0/
Data availability:
Comments
Comment on this article
Sign in to comment
scite_
Similar content
1,656
Nusinersen in adolescents and young adults with SMA: longitudinal experience from an expanded cohort of CS2/CS12 and SHINE participants. World Muscle Society Virtual Congress
Authors:
BT Darras
,
JW Day
,
KJ Swoboda
Nusinersen in the treatment of spinal muscular atrophy
Authors:
K. Goodkey
,
T. Aslesh
,
R. Maruyama
…
Nusinersen: evidence of sustained clinical improvement and lessened fatigue in older ambulatory patients with spinal muscular atrophy
Authors:
Hugh J. McMillan
See all similar
Cited by
359
Advances in oligonucleotide drug delivery
Authors:
Thomas C Roberts
,
Robert (Bob) Langer
,
Matthew Wood
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Authors:
Richard Finkel
,
Eugenio Mercuri
,
Basil Darras
…
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
Authors:
Eugenio Mercuri
,
Basil Darras
,
Claudia A. Chiriboga
…
See all cited by
Version 1
Version 1