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CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia
Author(s):
Haydar Frangoul
,
David Altshuler
,
M Cappellini
,
Yi-Shan Chen
,
Jennifer Domm
,
Brenda K Eustace
,
Juergen L Foell
,
Josu de la Fuente
,
Stephan Grupp
,
Rupert Handgretinger
,
Tony Ho
,
Antonis Kattamis
,
Andrew Kernytsky
,
Julie A. Lekstrom-Himes
,
Amanda M Li
,
Franco Locatelli
,
Markus Mapara
,
Mariane de Montalembert
,
Damiano Rondelli
,
Akshay Sharma
,
Sujit Sheth
,
Sandeep Soni
,
Martin Steinberg
,
Donna Wall
,
Angela Yen
,
Selim Corbacioglu
Publication date:
2020-12-05
Journal:
New England Journal of Medicine
Publisher:
Massachusetts Medical Society
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PubMed
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CRISPR/Cas9 editing in human blood
Author and article information
Journal
DOI::
10.1056/NEJMoa2031054
PubMed ID::
33283989
License:
http://www.nejmgroup.org/legal/terms-of-use.htm
Data availability:
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